Pharmacokinetics of therapies approved for spinal muscular atrophy: A narrative review of current evidence.

Sel E. K., Gkrinia E. M. M., Roncato R., Vitezić D., Janković S., Belančić A.

The Journal of international medical research, vol.53, no.11, 2025 (SCI-Expanded, Scopus)

  • Publication Type: Article / Article
  • Volume: 53 Issue: 11
  • Publication Date: 2025
  • Doi Number: 10.1177/03000605251397777
  • Journal Name: The Journal of international medical research
  • Journal Indexes: Science Citation Index Expanded (SCI-EXPANDED), Scopus, BIOSIS, EMBASE, Directory of Open Access Journals
  • Keywords: Spinal muscular atrophy, pharmacokinetics, disease-modifying therapies, nusinersen, onasemnogene abeparvovec, risdiplam
  • Dokuz Eylül University Affiliated: Yes